Mapping and Evaluating Delivery Methods for Gene
Editing in Clinical Applications
GeneHumdi COST Action’s Working Group 3 (Delivery) and Working Group 5 (Translation into the clinic) are hosting a joint meeting in Ankara (Turkey) on September 25th!
This key event will bring together experts to review the latest progress in delivery technologies, including viral methods like AAV vectors and non-viral systems such as nanoparticles and EVs. The groups will also focus on the critical steps of translating these therapies from the lab to patient care, addressing crucial topics like GMP scale-up, regulatory considerations, and strategies to accelerate clinical implementation. By fostering collaboration and sharing knowledge, the meeting aims to enhance the safety, efficiency, and scalability of gene editing therapies, ultimately speeding up the journey from research to effective clinical solutions for genetic diseases.
The meeting hosted by Dusko Lainscek, will revolve around four major topics:
Dive into Delivery Tech: We’ll explore the latest ways to get gene-editing tools where they need to go. We’re talking about everything from tried-and-true AAV vectors to cutting-edge stuff like nanoparticles, VLPs, and EVs. The goal is to figure out the pros, cons, and biggest hurdles for each method.
The Journey From Lab to Bedside: Let’s get real about what it takes to turn lab research into actual treatments. We’ll look at real-world examples, like liver-directed gene editing, and discuss how we can get these therapies ready for mass production (GMP scale-up) while navigating all the tricky regulatory rules.
Major hurdles for delivery systems: We’ll have a series of roundtables to brainstorm solutions for the biggest challenges facing gene editing today. This is a chance to openly discuss what’s holding us back and find new opportunities to move the field forward.
Connect and Collaborate: This meeting is a prime opportunity to network with the people who are shaping the future of medicine. You’ll get to meet and chat with researchers, doctors, regulators, and industry leaders to build connections that could lead to some seriously cool collaborations
This Meeting is held in Ankara ( Turkey) thanks to The LÖSEV Foundation for Children with Leukemia and LÖSANTE Hospital .
Learn how to participate in the venue or online: Download the full program!
We´ll meet in Ankara !
